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RECRUITING
Updated: Oct 31, 2025
HABIT-ILE + FST in Children With SMA
Phase
N/A
Early 1
1
2
3
4
Brief Summary
This single-arm pilot study will assess the feasibility and preliminary effectiveness of an intensive motor skill intervention (HABIT-ILE) combined with functional strength training (FST) in children with SMA who are receiving disease-modifying therapies. Participants will attend one 6-hour HABIT-ILE + FST session each weekend (Saturday or Sunday) for 15 weeks, for a total of 90 hours of training. Feasibility will be evaluated through questionnaires, and effectiveness through standardized motor function assessments.
Key Information
Participation Criteria
Study Design
Locations & Contacts
Inclusion Criteria:
- Diagnosis of SMA
- Able to participate in all pre and post intervention assessments
- Able to understand and speak English
- Able to understand directions (no significant cognitive delay or serious behavioral issues that would limit participation)
- Receiving a stable dose of disease-modifying therapies for at least 6 months prior to enrollment.
Exclusion Criteria:
- Orthopedic surgery within the last year (confound)
- Initiation of any new pharmaceutical treatment during the study period
- Participation in a clinical trial of an investigational therapy